Product Candidate
Disease Indication
Current Stage of Development
Delayed release, enteric-coated cysteamine bitartrate (DR Cysteamine)
Nephropathic Cystinosis
Phase II (ongoing, open IND ) Orphan Product Designation
DR Cysteamine
Non-Alcoholic Steatohepatitis (NASH)
Phase IIa (pending, open IND)
Huntington’s Disease
Phase II (planned)
Batten Disease
Convivia™
Aldehyde Dehydrogenase (ALDH2) Deficiency
Phase IIa (planned, IND filed)
HepTide™
Hepatocellular Carcinoma (HCC)
Preclinical (ongoing)
Hepatitis C
WntTide™
Breast Cancer
NeuroTrans™
Neurodegenerative Diseases